Company Performance Metrics
- Nick Leschly: CEOPast Role: Third Rock Ventures, Partner
Ilya Shestopalov: DirectorPast Role: Genetix Biotherapeutics Inc., Senior Scientist
Genetix Biotherapeutics is a privately-held, commercial-stage biotechnology company dedicated to delivering potentially curative genetic therapies for patients living with severe rare diseases.The company focuses on developing and commercializing one-time administered gene therapies that directly treat the underlying genetic cause of the disease.
They currently have FDA-approved treatments for:Sickle Cell Disease (Product: LYFGENIA)$\beta$-thalassemia (Product: ZYNTEGLO)Cerebral Adrenoleukodystrophy (CALD) (Product: SKYSONA)With a foundation of over 30 years of genetic therapy innovation, Genetix Biotherapeutics is committed to scaling patient access, commercial execution, and improving the overall treatment experience for patients and healthcare providers.
